Systemic delivery of morpholino oligonucleotide restores dystrophin expression bodywide and improves dystrophic pathology

Julia Alter, Fang Lou, Adam Rabinowitz, Hai Fang Yin, Jeffrey Rosenfeld, Steve D. Wilton, Terence A. Partridge, Long Lu Qi

Research output: Contribution to journalArticlepeer-review

Original languageEnglish
Pages (from-to)175-177
Number of pages3
JournalNature Medicine
Volume12
Issue number2
DOIs
StatePublished - Mar 14 2006

ASJC Scopus Subject Areas

  • General Biochemistry,Genetics and Molecular Biology

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