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Resolving the Unresolvable: Nanopore Sequencing as a Comprehensive Quality Control Platform for Gene Therapy Vectors

  • Yan Xu
  • , Xiao Bing Zhang
  • , Jian Ping Zhang

Research output: Contribution to journal › Review article › peer-review

Original languageEnglish
Pages (from-to)991-1007
Number of pages17
JournalHuman Gene Therapy
Volume37
Issue number21-22
DOIs
StatePublished - Nov 2025
Externally publishedYes

ASJC Scopus Subject Areas

  • Molecular Medicine
  • Molecular Biology
  • Genetics

Keywords

  • adeno-associated virus (AAV)
  • mRNA therapeutics
  • nanopore sequencing
  • poly(A) tail
  • quality control (CMC)

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