Real-world Adherence to Nusinersen in Adults with Spinal Muscular Atrophy in the US: A Multi-site Chart Review Study

  • Lauren Elman
  • , Bora Youn
  • , Crystal M. Proud
  • , Margaret R. Frey
  • , Senda Ajroud-Driss
  • , M. Eileen McCormick
  • , David Michelson
  • , Michael S. Cartwright
  • , Terry Heiman-Patterson
  • , Joseph M. Choi
  • , Aastha Chandak
  • , Artak Khachatryan
  • , Marta Martinez
  • , Angela D. Paradis

Research output: Contribution to journalArticlepeer-review

Original languageEnglish
Pages (from-to)655-660
Number of pages6
JournalJournal of Neuromuscular Diseases
Volume9
Issue number5
DOIs
StatePublished - 2022

ASJC Scopus Subject Areas

  • Neurology
  • Clinical Neurology

Keywords

  • Medication adherence
  • adults
  • antisense oligonucleotides
  • neuromuscular diseases
  • retrospective studies
  • spinal muscular atrophy

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