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Operational Development and Launch of an Adaptive Platform Trial in Amyotrophic Lateral Sclerosis: Processes and Learnings From the First Four Regimens of the HEALEY ALS Platform Trial

  • for the Healey ALS Platform Trial Study Group

Research output: Contribution to journalArticlepeer-review

Original languageEnglish
Pages (from-to)294-305
Number of pages12
JournalMuscle & Nerve
Volume72
Issue number2
DOIs
StatePublished - Aug 2025

ASJC Scopus Subject Areas

  • Physiology
  • Clinical Neurology
  • Cellular and Molecular Neuroscience
  • Physiology (medical)

Keywords

  • HEALEY ALS platform trial
  • adaptive platform trials
  • amyotrophic lateral sclerosis
  • clinical operations
  • motor neuron disease

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