Modulation of Immune Reaction in Hydrodynamic Gene Therapy for Hemophilia A

  • Mei Zhao
  • , Yi Dan Sun
  • , Mengdi Yin
  • , Juan Juan Zhao
  • , Si Ang Li
  • , Guohua Li
  • , Feng Zhang
  • , Jing Xu
  • , Fei Ying Meng
  • , Beldon Zhang
  • , Xin Yu Sun
  • , Jian Ping Zhang
  • , Tao Cheng
  • , Xiao Bing Zhang

Research output: Contribution to journalArticlepeer-review

Original languageEnglish
Pages (from-to)404-420
Number of pages17
JournalHuman Gene Therapy
Volume33
Issue number7-8
DOIs
StatePublished - Apr 2022

ASJC Scopus Subject Areas

  • Molecular Medicine
  • Molecular Biology
  • Genetics

Keywords

  • CRISPR-Cas9
  • genome editing
  • hemophilia A
  • plasmids

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