Leveraging CRISPR-Cas9 for Accurate Detection of AAV-Neutralizing Antibodies: The AAV-HDR Method

  • Guohua Li
  • , Saining Tian
  • , Xinyu Sun
  • , Mei Zhao
  • , Feng Zhang
  • , Jian Ping Zhang
  • , Tao Cheng
  • , Xiao Bing Zhang

Research output: Contribution to journalArticlepeer-review

Original languageEnglish
Pages (from-to)490-505
Number of pages16
JournalHuman Gene Therapy
Volume35
Issue number13-14
DOIs
StatePublished - Jul 1 2024
Externally publishedYes

ASJC Scopus Subject Areas

  • Molecular Medicine
  • Molecular Biology
  • Genetics

Keywords

  • AAV homologous recombination (AAV-HDR)
  • AAV overexpression (AAV-OE)
  • AAV vector
  • AAV-neutralizing antibody
  • CRISPR-Cas9
  • NT50

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