Gene therapy for adenosine deaminase-deficient severe combined immune deficiency: Clinical comparison of retroviral vectors and treatment plans

Fabio Candotti; Kit L. Shaw; Linda Muul; Denise Carbonaro; Robert Sokolic; Christopher Choi; Shepherd H. Schurman; Elizabeth Garabedian; Chimene Kesserwan; G. Jayashree Jagadeesh; Pei Yu Fu; Eric Gschweng; Aaron Cooper; John F. Tisdale; Kenneth I. Weinberg; Gay M. Crooks; Neena Kapoor; Ami Shah; Hisham Abdel-Azim; Xiao Jin Yu; Monika Smogorzewska; Alan S. Wayne; Howard M. Rosenblatt; Carla M. Davis; Celine Hanson; Radha G. Rishi; Xiaoyan Wang; David Gjertson; Otto O. Yang; Arumugam Balamurugan; Gerhard Bauer; Joanna A. Ireland; Barbara C. Engel; Gregory M. Podsakoff; Michael S. Hershfield; R. Michael Blaese; Robertson Parkman; Donald B. Kohn

doi:10.1182/blood-2012-02-400937

Gene therapy for adenosine deaminase-deficient severe combined immune deficiency: Clinical comparison of retroviral vectors and treatment plans

Fabio Candotti, Kit L. Shaw, Linda Muul, Denise Carbonaro, Robert Sokolic, Christopher Choi, Shepherd H. Schurman, Elizabeth Garabedian, Chimene Kesserwan, G. Jayashree Jagadeesh, Pei Yu Fu, Eric Gschweng, Aaron Cooper, John F. Tisdale, Kenneth I. Weinberg, Gay M. Crooks, Neena Kapoor, Ami Shah, Hisham Abdel-Azim, Xiao Jin YuMonika Smogorzewska, Alan S. Wayne, Howard M. Rosenblatt, Carla M. Davis, Celine Hanson, Radha G. Rishi, Xiaoyan Wang, David Gjertson, Otto O. Yang, Arumugam Balamurugan, Gerhard Bauer, Joanna A. Ireland, Barbara C. Engel, Gregory M. Podsakoff, Michael S. Hershfield, R. Michael Blaese, Robertson Parkman, Donald B. Kohn

Research output: Contribution to journal › Article › peer-review

Original language	English
Pages (from-to)	3635-3646
Number of pages	12
Journal	Blood
Volume	120
Issue number	18
DOIs	https://doi.org/10.1182/blood-2012-02-400937
State	Published - Nov 1 2012
Externally published	Yes

ASJC Scopus Subject Areas

Biochemistry
Immunology
Hematology
Cell Biology

Access to Document

10.1182/blood-2012-02-400937

OpenUrl availability

Full text

Cite this

Candotti, F., Shaw, K. L., Muul, L., Carbonaro, D., Sokolic, R., Choi, C., Schurman, S. H., Garabedian, E., Kesserwan, C., Jagadeesh, G. J., Fu, P. Y., Gschweng, E., Cooper, A., Tisdale, J. F., Weinberg, K. I., Crooks, G. M., Kapoor, N., Shah, A., Abdel-Azim, H., ... Kohn, D. B. (2012). Gene therapy for adenosine deaminase-deficient severe combined immune deficiency: Clinical comparison of retroviral vectors and treatment plans. Blood, 120(18), 3635-3646. https://doi.org/10.1182/blood-2012-02-400937

Candotti, F, Shaw, KL, Muul, L, Carbonaro, D, Sokolic, R, Choi, C, Schurman, SH, Garabedian, E, Kesserwan, C, Jagadeesh, GJ, Fu, PY, Gschweng, E, Cooper, A, Tisdale, JF, Weinberg, KI, Crooks, GM, Kapoor, N, Shah, A, Abdel-Azim, H, Yu, XJ, Smogorzewska, M, Wayne, AS, Rosenblatt, HM, Davis, CM, Hanson, C, Rishi, RG, Wang, X, Gjertson, D, Yang, OO, Balamurugan, A, Bauer, G, Ireland, JA, Engel, BC, Podsakoff, GM, Hershfield, MS, Blaese, RM, Parkman, R & Kohn, DB 2012, 'Gene therapy for adenosine deaminase-deficient severe combined immune deficiency: Clinical comparison of retroviral vectors and treatment plans', Blood, vol. 120, no. 18, pp. 3635-3646. https://doi.org/10.1182/blood-2012-02-400937

@article{65221d22fce747938083a5e496542d88,

title = "Gene therapy for adenosine deaminase-deficient severe combined immune deficiency: Clinical comparison of retroviral vectors and treatment plans",

author = "Fabio Candotti and Shaw, {Kit L.} and Linda Muul and Denise Carbonaro and Robert Sokolic and Christopher Choi and Schurman, {Shepherd H.} and Elizabeth Garabedian and Chimene Kesserwan and Jagadeesh, {G. Jayashree} and Fu, {Pei Yu} and Eric Gschweng and Aaron Cooper and Tisdale, {John F.} and Weinberg, {Kenneth I.} and Crooks, {Gay M.} and Neena Kapoor and Ami Shah and Hisham Abdel-Azim and Yu, {Xiao Jin} and Monika Smogorzewska and Wayne, {Alan S.} and Rosenblatt, {Howard M.} and Davis, {Carla M.} and Celine Hanson and Rishi, {Radha G.} and Xiaoyan Wang and David Gjertson and Yang, {Otto O.} and Arumugam Balamurugan and Gerhard Bauer and Ireland, {Joanna A.} and Engel, {Barbara C.} and Podsakoff, {Gregory M.} and Hershfield, {Michael S.} and Blaese, {R. Michael} and Robertson Parkman and Kohn, {Donald B.}",

year = "2012",

month = nov,

day = "1",

doi = "10.1182/blood-2012-02-400937",

language = "English",

volume = "120",

pages = "3635--3646",

journal = "Blood",

issn = "0006-4971",

number = "18",

}

TY - JOUR

T1 - Gene therapy for adenosine deaminase-deficient severe combined immune deficiency

T2 - Clinical comparison of retroviral vectors and treatment plans

AU - Candotti, Fabio

AU - Shaw, Kit L.

AU - Muul, Linda

AU - Carbonaro, Denise

AU - Sokolic, Robert

AU - Choi, Christopher

AU - Schurman, Shepherd H.

AU - Garabedian, Elizabeth

AU - Kesserwan, Chimene

AU - Jagadeesh, G. Jayashree

AU - Fu, Pei Yu

AU - Gschweng, Eric

AU - Cooper, Aaron

AU - Tisdale, John F.

AU - Weinberg, Kenneth I.

AU - Crooks, Gay M.

AU - Kapoor, Neena

AU - Shah, Ami

AU - Abdel-Azim, Hisham

AU - Yu, Xiao Jin

AU - Smogorzewska, Monika

AU - Wayne, Alan S.

AU - Rosenblatt, Howard M.

AU - Davis, Carla M.

AU - Hanson, Celine

AU - Rishi, Radha G.

AU - Wang, Xiaoyan

AU - Gjertson, David

AU - Yang, Otto O.

AU - Balamurugan, Arumugam

AU - Bauer, Gerhard

AU - Ireland, Joanna A.

AU - Engel, Barbara C.

AU - Podsakoff, Gregory M.

AU - Hershfield, Michael S.

AU - Blaese, R. Michael

AU - Parkman, Robertson

AU - Kohn, Donald B.

PY - 2012/11/1

Y1 - 2012/11/1

UR - http://www.scopus.com/inward/record.url?scp=84868589740&partnerID=8YFLogxK

UR - http://www.scopus.com/inward/citedby.url?scp=84868589740&partnerID=8YFLogxK

U2 - 10.1182/blood-2012-02-400937

DO - 10.1182/blood-2012-02-400937

M3 - Article

C2 - 22968453

AN - SCOPUS:84868589740

SN - 0006-4971

VL - 120

SP - 3635

EP - 3646

JO - Blood

JF - Blood

IS - 18

ER -

Gene therapy for adenosine deaminase-deficient severe combined immune deficiency: Clinical comparison of retroviral vectors and treatment plans

ASJC Scopus Subject Areas

Access to Document

OpenUrl availability

Other files and links

Cite this