Enhancing hemophilia A gene therapy by strategic F8 deletions in AAV vectors

Juan Juan Zhao, Sai Ning Tian, Xiang Li, Zu Yi Peng, Guo Hua Li, Feng Zhang, Mei Zhao, Jian Ping Zhang, Xiao Bing Zhang

Research output: Contribution to journalArticlepeer-review

Original languageEnglish
Pages (from-to)e00217
JournalBlood Science
Volume7
Issue number1
DOIs
StatePublished - Feb 11 2025
Externally publishedYes

ASJC Scopus Subject Areas

  • Hematology

Keywords

  • Adeno-associated viruses (AAV)
  • BDDF8
  • Gene therapy
  • Hemophilia A

Cite this