Biomembrane-inspired lipid nanoparticles enhance CRISPR-Cas9 editing for hemophilia A

  • Juan Juan Zhao
  • , Sai Ning Tian
  • , Zu Yi Peng
  • , Jia Xin Ren
  • , Yang Yang Zhang
  • , Guo Hua Li
  • , Dong Hao Deng
  • , Jian Ping Zhang
  • , Xiao Bing Zhang

Research output: Contribution to journalArticlepeer-review

Original languageEnglish
Article number114141
JournalJournal of Controlled Release
Volume386
DOIs
StatePublished - Oct 10 2025
Externally publishedYes

ASJC Scopus Subject Areas

  • Pharmaceutical Science

Keywords

  • Biomembrane-inspired lipid nanoparticles
  • C18-galactosyl ceramide (C18-GalCer)
  • CRISPR-Cas9 delivery
  • Freeze-thaw stability
  • Hemophilia A
  • Hepatic RNA delivery
  • Sphingomyelin

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