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AviNP-Seq: A Blindspot-Free Single-Molecule Framework for Unmasking AAV Genome Heterogeneity and Determining Packaging Limits

  • Guo Hua Li
  • , Yan Xu
  • , Tong Liu
  • , Xiao Yu Ma
  • , Meng Ting Hou
  • , Shan Chen Pang
  • , Jian Ping Zhang
  • , Tao Cheng
  • , Xiao Bing Zhang

Research output: Contribution to journal › Article › peer-review

Original languageEnglish
Pages (from-to)887-902
Number of pages16
JournalHuman Gene Therapy
Volume37
Issue number17-18
DOIs
StatePublished - Sep 2026
Externally publishedYes

ASJC Scopus Subject Areas

  • Molecular Medicine
  • Molecular Biology
  • Genetics

Keywords

  • RNP
  • clustered regularly interspaced short palindromic repeats (CRISPR)-Cas9
  • library preparation bias
  • nanopore long-read sequencing
  • recombinant adeno-associated virus (rAAV)

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