β-globin gene transfer to human bone marrow for sickle cell disease

  • Zulema Romero
  • , Fabrizia Urbinati
  • , Sabine Geiger
  • , Aaron R. Cooper
  • , Jennifer Wherley
  • , Michael L. Kaufman
  • , Roger P. Hollis
  • , Rafael Ruiz De Assin
  • , Shantha Senadheera
  • , Arineh Sahagian
  • , Xiangyang Jin
  • , Alyse Gellis
  • , Xiaoyan Wang
  • , David Gjertson
  • , Satiro DeOliveira
  • , Pamela Kempert
  • , Sally Shupien
  • , Hisham Abdel-Azim
  • , Mark C. Walters
  • , Herbert J. Meiselman
  • Rosalinda B. Wenby, Theresa Gruber, Victor Marder, Thomas D. Coates, Donald B. Kohn

Research output: Contribution to journalArticlepeer-review

Original languageEnglish
Pages (from-to)3317-3330
Number of pages14
JournalJournal of Clinical Investigation
Volume123
Issue number8
DOIs
StatePublished - Aug 1 2013
Externally publishedYes

ASJC Scopus Subject Areas

  • General Medicine

Cite this